天使综合征药物研究进展汇总
clinicaltrials
- Promoting Prosocial Behavior in Syndromic Intellectual and Developmental Disabilities
- Angelman Natural History Study - FAST Spain
- IDMet (RaDiCo Cohort) (RaDiCo-IDMet)
- Development of a Newborn Screening Assay for Angelman Syndrome and Prader-Willi Syndrome
- Angelman Syndrome Video Assessment (ASVA) Source Material Study
- Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype.
- Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype
- The Global Angelman Syndrome Registry
- HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
- Angelman Syndrome Natural History Study-FAST UK
- Angelman Syndrome Natural History Study- FAST UK
- An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
- A Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants
- Ghrelin in Patients With a Rare Disease Associated With Intellectual Disability, and Hyperphagia, and/or Overweight, and/or Obesity
- Angelman Syndrome Natural History Study
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