天使综合征药物研究进展汇总
clinicaltrials
- Development of a Newborn Screening Assay for Angelman Syndrome and Prader-Willi Syndrome
- Angelman Syndrome Video Assessment (ASVA) Source Material Study
- Study to Investigate the Pharmacokinetics and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype
- The Global Angelman Syndrome Registry
- HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
- Angelman Syndrome Natural History Study-FAST UK
- Angelman Syndrome Natural History Study- FAST UK
- An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
- A Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants
- Angelman Syndrome Natural History Study
- A Study To Investigate The Safety, Tolerability, Pharmacokinetics And Pharmacodynamics Of RO7248824 In Participants With Angelman Syndrome
- A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome
- Diagnosis of Prader-Willi Syndrome and Angelman Syndrome
- Angelman Syndrome (AS) Biomarker Study
- An Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman Syndrome
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